Background: BRAF/MEK inhibitor therapy has demonstrated PFS and OS benefits and is standard of care for the treatment of advanced BRAF V600-mutant melanoma. We report a 5-yr update from the COLUMBUS trial.
Methods: In Part 1 of COLUMBUS, 577 pts with advanced/metastatic BRAF V600-mutant melanoma, untreated or progressed after first-line immunotherapy, were randomized 1:1:1 to encorafenib 450mg QD + binimetinib 45mg BID (COMBO450), encorafenib 300mg QD (ENCO300), or vemurafenib 960mg BID (VEM). An updated analysis including PFS, OS, ORR (by blinded independent central review), and safety was conducted after minimum follow-up of 65.2 m.
Results: At data cut-off (Sep 15, 2020), there were 131 (68%), 117 (60%), and 145 (76%) deaths in the COMBO450, ENCO300, and VEM treatment arms, respectively. For COMBO450, ENCO300, and VEM, the 5-year OS rate was 34.7%, 34.9%, and 21.4%, and median OS rates were 33.6, 23.5 and 16.9 months respectively (median follow-up: 70.4m). The 5-yr OS rate (95% CI) in COMBO450 pts who had normal LDH levels at baseline was 45.1% (36.5–53.2). For COMBO450, ENCO300, and VEM, the 5-year PFS rate was 22.9%, 19.3%, and 10.2%; ORR (95% CI) was 64.1% (56.8–70.8), 51.5% (44.3–58.8), and 40.8% (33.8–48.2); and the median duration of response (DOR) was 18.6, 15.5, and 12.3m, respectively. Safety results were consistent with the known tolerability profile of COMBO450. Additional efficacy and updated safety analyses will be presented. Following study drug discontinuation, the most common subsequent treatment in all arms was checkpoint inhibitors.
Conclusions: Updated OS and DOR COMBO450 results demonstrate continued long-term benefits in pts with BRAF V600-mutant melanoma. Clinical trial information: NCT01909453.